Gene therapy replaces a faulty gene or adds a new gene to correct the mutation (genetic fault).

Gene (or genome) editing is a type of gene therapy, that involves the insertion, deletion or replacement of DNA at a specific site in the genome of an organism or cell. It is usually achieved in the lab using engineered nucleases also known as ‘molecular scissors’.

Gene therapy projects

Current Projects, Gene Therapy, Quality of Life Change, Whole Body Treatment

Gene editing projects

Cure EB
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