Editing of RDEB fibroblasts
Testing the in vivo efficacy of base and prime editing in primary fibroblasts and in a 3D skin model of dystrophic epidermolysis bullosa...
Testing the in vivo efficacy of base and prime editing in primary fibroblasts and in a 3D skin model of dystrophic epidermolysis bullosa...
Testing the efficacy of genomic base editing in dystrophic epidermolysis bullosa primary fibroblasts...
Development of a topical gene-editing treatment to restore Collagen VII...
Combined respiratory epithelial cell and gene therapy for amelioration of respiratory symptoms in children with Junctional Epidermolysis Bullosa...
Pre-clinical and clinical trial for using gene-edited skin in Recessive Dystrophic Epidermolysis Bullosa...
A nanoneedle bandage for topical intracellular COL7A1 gene therapy to accelerate wound healing in RDEB...
Phase I/II ex vivo gene therapy clinical trial for RDEB using genetically corrected autologous skin equivalent grafts...
Next generation genome editing for Recessive Dystrophic Epidermolysis Bullosa...
Stem cell regeneration of the ocular surface in Recessive Dystrophic Epidermolysis Bullosa...
Phase I study of lentiviral-mediated COL7A1 gene-modified autologous fibroblasts in adults with Recessive Dystrophic Epidermolysis Bullosa...