mRNA-based base editing
Evaluation of long-term effect on skin homeostasis and regeneration in a RDEB mouse model ...
Evaluation of long-term effect on skin homeostasis and regeneration in a RDEB mouse model ...
The project aims to develop a strategy that could be used to treat a significant subset of RDEB patients carrying selected mutations....
Study of the Safety, Tolerability, and Efficacy of an iPS Cell-based Therapy for RDEB...
PASTE-Mediated Superexon Replacement of COL7A1 as a Treatment for Dystrophic Epidermolysis Bullosa...
Testing the in vivo efficacy of base and prime editing in primary fibroblasts and in a 3D skin model of dystrophic epidermolysis bullosa...
Testing the efficacy of genomic base editing in dystrophic epidermolysis bullosa primary fibroblasts...
Pre-clinical and clinical trial for using gene-edited skin in Recessive Dystrophic Epidermolysis Bullosa...
Gene editing for Epidermolysis Bullosa...
Epidermolysis Bullosa Therapeutic Reprogramming Consortium...
Next generation genome editing for Recessive Dystrophic Epidermolysis Bullosa...