Research Portfolio
Key
Gene therapy and 
Gene editing
Cell therapy
Drug therapy
Protein therapy
EB cancer therapy
Research
2016
Lenticol F
Phase I study of lentiviral-mediated COL7A1 gene-modified autologous fibroblasts in adults with Recessive Dystrophic Epidermolysis Bullosa
ADSTEM
A phase I/II study to evaluate allogeneic mesenchymal stromal cells for the treatment of skin disease in adults with Recessive Dystrophic Epidermolysis Bullosa
2015
Limbal stem cells
Limbal stem cells for treatment of corneal wounds in Epidermolysis Bullosa
2014
TALEN-based gene editing
A TALEN-based approach to developing safer, more effective treatments for people with Epidermolysis Bullosa
2013
EBSTEM
Clinical trial of mesenchymal stromal cells in Recessive Dystrophic Epidermolysis Bullosa