Research Portfolio
Key
Gene therapy and 
Gene editing
Cell therapy
Drug therapy
Protein therapy
EB cancer therapy
Research
NanoCol
A nanoneedle bandage for topical intracellular COL7A1 gene therapy to accelerate wound healing in Recessive Dystrophic Epidermolysis Bullosa
Exon skipping approach to RDEB
Exon skipping approach to Recessive Dystrophic Epidermolysis Bullosa
FIBRX Derm
Development of a topical gel formulation of decorin to reduce fibrosis
Mission EB
Double blind placebo controlled study of mesenchymal intravenous stromal cell infusions in children with Recessive Dystrophic Epidermolysis Bullosa
RNA Derm
Development of IV-administered siRNAs targeting mutant KRT5 and KRT1 in EB Simplex
TXA127
Development of an oral formulation of the peptide angiotensin-(1-7) to reduce fibrosis
EBGRAFT
Phase I/II ex vivo gene therapy clinical trial for RDEB using autologous skin equivalent grafts genetically corrected with a COL7A1-encoding SIN retroviral vector
Gene editing for EB
Gene editing for Epidermolysis Bullosa
Next generation genome editing
Next generation genome editing for Recessive Dystrophic Epidermolysis Bullosa
EB iPS Consortium
Epidermolysis Bullosa Therapeutic Reprogramming Consortium