Research Portfolio
Key
Gene therapy and 
Gene editing
Cell therapy
Drug therapy
Protein therapy
EB cancer therapy
Research
ELK-003
An opthalmic solution for the treatment of corneal abrasions associated with epidermolysis bullosa
mRNA-based base editing
Evaluation of long-term effect on skin homeostasis and regeneration in a RDEB mouse model using different delivery methods of LNPs encapsulating mRNA-based base editing approach
Bespoke Therapy for RDEB
Bespoke antisense oligomer-mediated splice modulating therapies for Recessive Dystrophic Epidermolysis Bullosa patients
Therapy for JEB Airway Disease
Towards cell and gene therapy for Junctional Epidermolysis Bullosa airway disease
Nova Anchora
Development of NvA-011 for topical application in Dystrophic Epidermolysis Bullosa
Base & Prime Editing for RDEB
Base and prime editing strategies for Recessive Dystrophic Epidermolysis Bullosa
Gene & Cell Therapy in RDEB SCC
Gene & Cell Therapy in Recessive Dystrophic Epidermolysis Squamous Cell Carcinoma
Nonsense Tx
Nonsense Tx reading through disease causing nonsense codons
PASTE gene therapy in DEB
PASTE-Mediated Superexon Replacement of COL7A1 as a Treatment for Dystrophic Epidermolysis Bullosa
Spray-on-Skin
Study of the Safety, Tolerability, and Efficacy of an iPS Cell-based Therapy for Recessive Dystrophic Epidermolysis Bullosa Delivered with a Spray-on-Skin Device