Gene therapy for airway disease
Combined respiratory epithelial cell and gene therapy for amelioration of respiratory symptoms in children with Junctional Epidermolysis Bullosa Read more...
Archive
RDEB gene-edited skin
Pre-clinical and clinical trial for using gene-edited skin in Recessive Dystrophic Epidermolysis Bullosa Read more...
NanoCol
A nanoneedle bandage for topical intracellular COL7A1 gene therapy to accelerate wound healing in Recessive Dystrophic Epidermolysis Bullosa Read more...
Mission EB
Double blind placebo controlled study of mesenchymal intravenous stromal cell infusions in children with Recessive Dystrophic Epidermolysis Bullosa Read more...
FIBRX Derm
Development of a topical gel formulation of decorin to reduce fibrosis Read more...
RNA Derm
Development of IV-administered siRNAs targeting mutant KRT5 and KRT1 in EB Simplex Read more...
TXA127
Development of an oral formulation of the peptide angiotensin-(1-7) to reduce fibrosis Read more...
EBGRAFT
Phase I/II ex vivo gene therapy clinical trial for RDEB using autologous skin equivalent grafts genetically corrected with a COL7A1-encoding SIN retroviral vector Read more...
Gene editing for EB
Gene editing for Epidermolysis Bullosa Read more...
EB iPS Consortium
Epidermolysis Bullosa Therapeutic Reprogramming Consortium Read more...