Base & Prime Editing for RDEB
Base and prime editing strategies for Recessive Dystrophic Epidermolysis Bullosa Read more...
Archive
Gene & Cell Therapy in RDEB SCC
Gene & Cell Therapy in Recessive Dystrophic Epidermolysis Squamous Cell Carcinoma Read more...
Spray-on-Skin
Study of the Safety, Tolerability, and Efficacy of an iPS Cell-based Therapy for Recessive Dystrophic Epidermolysis Bullosa Delivered with a Spray-on-Skin Device Read more ...
Exon skipping approach to RDEB
Exon skipping approach to Recessive Dystrophic Epidermolysis Bullosa Read more...
siRNA interference in EBS
siRNA-mediated allele-specific inhibition of mutant KRT5 and KRT14 transcripts carrying frequent dominant mutations in Epidermolysis Bullosa Simplex Read more...
PASTE gene therapy in DEB
PASTE-Mediated Superexon Replacement of COL7A1 as a Treatment for Dystrophic Epidermolysis Bullosa Read more...
Rigosertib for RDEB SCC
Rigosertib for recessive dystrophic epidermolysis bullosa-associated squamous cell carcinoma Read more...
Editing of RDEB fibroblasts
Testing the in vivo efficacy of base and prime editing in primary fibroblasts and in a 3D skin model of dystrophic epidermolysis bullosa Read more...
Base editing of RDEB fibroblasts
Testing the efficacy of genomic base editing in dystrophic epidermolysis bullosa primary fibroblasts Read more...
BrB-101
Development of a topical gene-editing treatment to restore Collagen VII Read more...